April 23 – 25, 2024
Boston, Massachusetts
Booth #325
Join Premier Research at the World Orphan Congress US for groundbreaking solutions, exclusive insights, and unmatched networking. Elevate your approach to rare diseases – visit our exhibit and be part of the future of orphan drug development!
Adam Bloomfield, M.D., Executive Director, Medical Affairs, Rare Diseases and Pediatrics, will be speaking on decentralized trials in pediatrics.
Unlocking Insights: How Decentralized Clinical Trials and Advanced Therapies Are Revolutionizing Pediatric Rare Disease Research
Wednesday, April 24, 11:25 – 11:45 a.m.
This session will explore solutions to challenges in pediatric rare disease research, specifically in consideration of decentralized clinical trials (DCT) and cell and gene therapy development. You will learn:
- The complexities of executing cell and gene therapy programs in pediatric populations
- Key considerations for instituting a DCT approach for cell and gene therapy programs in a pediatric population
- Strategies for seamless operationalization of DCTs