Gene Therapy for Rare Disorders US

March 20-23, 2023

Boston, MA

Booth #14

Visit Premier Research at booth #14 at Gene Therapy for Rare Disorders.

As the gene therapy field continues to break records, there are still significant challenges to overcome related to safety, efficacy, and accessibility. Learn how we can address the regulatory, clinical, manufacturing and pricing bottlenecks to progress gene therapies into and through the clinic.

Meet our speaker: Ken Ndugga-Kabuye, MD, FACMG, Vice President, Cell & Gene Therapy

He will be presenting on:

Rare “Plus”: The Operational Nuances to Consider When Designing Gene Therapy First-In-Human Studies

  • Design and safety considerations
  • Site selection considerations
  • Effective patient enrollment and ongoing engagement

March 21st, 11:15 A.M

Stream – CLINICAL – Designing & Implementing a Safe Clinical Trial