Rare Disease Research Embraces the Unknown. Let’s Take It On. Together.

Premier Research is built on a foundation of rare disease research.

With decades of relevant experience in developing novel therapies, devices, and diagnostics, we make rare a common focus. Our aim is to provide Sponsors of novel rare disease therapies with proactive solutions to ensure trials stay on course and fast-track clinical outcomes to deliver innovative medicines faster.

An estimated 400 million people worldwide are afflicted with over 10,000 rare diseases, approximately 95% of which do not have an available treatment. In the complex and uncharted territory of rare disease research, particularly cell and gene studies, Premier offers significant experience with natural history studies, precision medicine, and real-world data planning, trial design, and regulatory strategy to guide rare disease product development. Partnered with our strong expertise in enrolling special patient populations and our ability to manage complicated logistics and CMC challenges, our aim is to provide Sponsors of novel rare disease therapies with proactive solutions to ensure trials stay on course.