Tag: registry studies

Clinical Research: Phase 1 - Phase 4

Registry and Natural History Studies: Vital, Contrasting Roles in Clinical Research

Both registry studies and natural history studies play important roles in rare disease research. Understanding the differences between the two types of studies and how they can be used to inform clinical development can help sponsors plan for success. Sound drug development requires a comprehensive understanding of the disease being treated. To design reliable clinical...

Clinical Research: Phase 1 - Phase 4

Natural History or Registry Study? Conducting Rare Disease Research

Sound drug development requires a comprehensive understanding of the disease being treated. To design reliable clinical studies and achieve meaningful outcome measures, researchers must apply known etiology and thorough knowledge of the disease’s progression. For rare diseases, this information is often minimal at best: patient numbers are small and historical data is spread across treating...