Clinical Research: Phase 1 - Phase 4
Pharmaceutical Outsourcing | Registries and Natural History Studies in Rare Disease Drug Development
Increasing emphasis on rare diseases has led to a greater need to accurately define the profile, characteristics, and outcomes of patients living with those conditions. The development of safe and effective treatments of rare diseases requires a deep understanding of the disease of interest, including its frequency, clinical features, risk factors, outcomes, burden, and evolution....