Patient and Stakeholder Engagement
PM360 – Patient Advocates Assume a Large Role as Orphan Drug Development Expands
“Rare disease” may be the biggest misnomer in the pharmaceutical industry. Around the world, 350 million people live with conditions classified as rare because each afflicts a relatively small segment of the population. In the U.S., 30 million—nearly one in 10 Americans—suffer from one of about 7,000 known rare diseases. As it applies to this...