September 13-14, 2023
Princeton, NJ
Booth #19
Join Premier Research at Clinical Trials in Rare Diseases, an event that will explore the challenges in clinical trials for orphan drugs and rare diseases, bringing together clinical operations professionals from across multiple therapeutic areas to discuss common obstacles and solutions. It will explore the benefits of early planning and engagement with regulatory authorities, the importance of working closely with patients and patient advocacy groups, recruiting and retaining patients for rare disease studies, and much more.
Hear from Leslie Wetherell, our Executive Director, Program Strategy, Rare Disease and Pediatrics, who will be presenting.
Moving the Needle in Rare Disease Trials: How to Optimize Study Design Without Breaking the Bank
Wednesday, September 13, 9:30 -10 a.m.
It’s no secret that rare disease trials encounter many obstacles from start to finish. With small patient populations, limited data on the disease, and patient enrollment and retention challenges, every component of the study protocol can significantly influence the success of the trial. These challenges, paired with ever-increasing clinical trial costs, can leave sponsors feeling overwhelming pressure to stretch their budgets without sacrificing the data they need for regulatory approval.
During this session, you will learn:
- Tangible tactics for reducing patient burden
- Centralized monitoring strategies to contain biotech spend without compromising data quality
- Ways to infuse technology and decentralized approaches to enhance the patient experience