Premier Insight 285 | When Regulatory Meets Operations: FIH Gene Therapy Study Hits Milestone Despite IND Challenges
Developing a novel gene therapy requires a level of comfort with change and unpredictability. The path to regulatory approval is rarely straightforward, and roadblocks can enter at any turn. Premier Research was approached by a sponsor of an adeno-associated virus (AAV)-based gene silencing technology to conduct a natural history study, with a goal to identify...